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Cardiology

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Research Frontiers in Gene Editing in Inherited Cardiomyopathies

Application of CRISPR-Cas9 and base editing technologies to correct genetic mutations causing hypertrophic and dilated cardiomyopathies.

Allele-Specific Silencing in Dominant Cardiomyopathy Pathogenesis
Prime Editing Precision at Sarcomeric Protein Hotspots
Epigenetic Rescue of Truncated Cardiac Tropomyosin Expression
Off-Target Effects in Myocardial Gene Correction Strategies
Temporal Delivery Windows for Fetal Cardiomyocyte Reprogramming
Base Editing Tolerance in Hypertrophic Cardiomyopathy Mutations
Compensatory Isoform Switching Following Dystrophin Gene Restoration
Immune Tolerance Mechanisms in Repeated Cardiac Gene Therapy
Mitochondrial DNA Editing in Maternal Inheritance Cardiomyopathies
Long-Term Phenotypic Reversion After in vivo Myocardial Correction

All Cardiology PhD categories